Validation of a Custom 30-Gene Probe-Capture Targeted Sequencing Panel to Detect Variants in FEVR-Linked Genes and the RS1 Gene

Document Type

Conference Proceeding

Publication Date

6-2025

Publication Title

Investigative Ophthalmology and Visual Science

Abstract

Purpose : To validate a novel custom 30-gene probe-capture panel that includes genes linked to FEVR, Norrie Disease, Persistent Fetal Vascular Syndrome, and XLRS (Retinoschisis). Samples previously sequenced with a custom Ampliseq 8-gene panel (NDP, FZD4, LRP5, TSPAN12, KIF11, CTNNB1, ZNF408, RS1) were reanalyzed against the 30-gene probe-capture workflow.

Methods : DNA sequencing was carried out with the Oakland University Institutional Review Board and Associated Retinal Consultants (ARC) IRB approval. Subjects were consented to the ARC Eye Biobank, and DNA-sequencing in the Eye Research Institute. Six genomic DNA samples that were previously sequenced with an 8-gene Ampliseq panel were resequenced using a custom 30-gene probe capture panel (Celemics). The 30-gene and 8-gene Illumina-compatible libraries were sequenced in-house on an Illumina iSeq-100 instrument. DNA samples were from different years and extracted with a manual or automated DNA extraction kit. Variant analysis employed the Ensembl Variant Effect Predictor, ClinVar, DbSNP, and GnomAD to categorize variant consequence and estimate variant frequency in the population.

Results : The probe-capture 30-gene panel successfully identified 100% of the variants previously detected by the Ampliseq 8-gene panel in the following genes: LRP5 (1 variant), ZNF408 (2 variants), RS1 (1 variant), and NDP (1 variant). In addition, the 30-gene probe capture approach uncovered several novel variants not identified in the previous sequencing, demonstrating an enhanced capacity to detect a broader range of potentially pathogenic variants. The panel also detected a previously known RS1 gene variant.

Conclusions : These test results demonstrate that the newer custom Celemics probe-capture 30-gene panel can replace the previous 8-gene panel used by our group for DNA sequencing of FEVR-related genes and the RS1 gene. The expanded 30-gene panel also includes several additional genes more recently linked to FEVR such as CTNND1, CTNNA1, and ECM1.

Volume

66

Issue

8

First Page

1837

Comments

ARVO (Association for Research in Vision and Ophthalmology) Annual Meeting, May 4-8, 2025, Salt Lake City, UT

Last Page

1837

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